Disorders of Somatic Mosaicism Sequencing

Overview

The Clinical Genomics Laboratory at WashU Medicine is a leader in the genetic diagnosis of disorders caused by somatic mosaicism. These conditions, which result from mosaic genetic changes, pose significant diagnostic challenges that the lab addresses using targeted gene panels with high-depth sequencing and expert interpretation. Panels are tailored to common clinical indications, including mosaic vascular malformations, overgrowth syndromes, cortical malformations with epilepsy, and inborn errors of immunity. Custom panels can also be configured to meet specific diagnostic needs.

Checklist

Available Tests and Gene Lists

Cortical Malformations and Epilepsy Panel

39 genes sequencedACTB, AKT1, AKT3, ARFGEF2, BRAF, CCM2, CCND2, CDKL5, DCX, DEPDC5, DYNC1H1, FLNA, GABRA1, GABRG2, GRIN2B, KCNQ2, KIF5C, MECP2, MTOR, NACC1, NPRL2, NPRL3, PAFAH1B1, PCDH19, PIK3CA, PIK3R2, PRKACA, PRKACB, PTEN, RHEB, RPS6, SCN1A, SCN2A, SLC35A2, SMO, TSC1, TSC2, TUBA1A and TUBB2B.

Inborn Errors of Immunity Panel

9 genes sequencedFAS, JAK1, KRAS, NRAS, PIK3CD, PIK3R1, STAT5B, TLR8 and UBA1.

Maffucci Syndrome Panel

2 genes sequenced: IDH1 and IDH2.

McCune Albright Syndrome Panel

5 genes sequencedGNAS, HRAS, KRAS, NF1 and NRAS

Nevus Panel

39 genes sequencedACTB, AKT1, AKT3, ARFGEF2, BRAF, CCM2, CCND2, CDKL5, DCX, DEPDC5, DYNC1H1, FLNA, GABRA1, GABRG2, GRIN2B, KCNQ2, KIF5C, MECP2, MTOR, NACC1, NPRL2, NPRL3, PAFAH1B1, PCDH19, PIK3CA, PIK3R2, PRKACA, PRKACB, PTEN, RHEB, RPS6, SCN1A, SCN2A, SLC35A2, SMO, TSC1, TSC2, TUBA1A and TUBB2B.

PIK3CA-Related Overgrowth Spectrum Disorders

FOCUSED PANEL
1 gene sequenced PIK3CA.

COMPREHENSIVE PANEL
75 genes sequencedACTB, ACVRL1, AKT1, AKT2, AKT3, ARAF, BRAF, CCBE1, CCM2, CCND2, CDKN1C, CELSR1, CLDN14, CTNNB1, DCHS1, ELMO2, ENG, EPHB4, FAT4, FGFR1, FGFR2, FLT4, FOXC2, GATA2, GDF2, GJA4, GJC2, GLMN, GNA11, GNA14, GNAQ, GNAS, HGF, HRAS, IDH1, IDH2, KDR, KEL, KIF11, KRAS, KRIT1, LZTR1, MAP2K1, MAP2K2, MAP3K3, MET, MTOR, NF1, NF2, NRAS, PDCD10, PDGFRB, PIEZO1, PIK3CA,  PIK3CD, PIK3R1, PIK3R2, PRKACA, PTEN, PTPN11, PTPN14, RASA1, RHOA, SHOC2, SMAD3, SMAD4, SMO, SOS1, SOX18, SPRED1, STAMBP, TEK, TSC1TSC2 and VEGFC.

Rasopathies Panel

26 genes sequencedBRAF, CBL, HRAS, KRAS, LZTR1, MAP2K1, MAP2K2, MAP3K3, MAP3K8, MRAS, NF1, NF2, NRAS, PPP1CB, PTPN11, RAF1, RASA1, RASA2, RIT1, RRAS2, SHOC2, SMAD4, SOS1, SOS2, SPRED1 and STAMBP.

Somatic Overgrowth Panel

49 genes sequencedACTB, AKT1, AKT2, AKT3, ARAF, BRAF, CCM2, CCND2, CDKN1C, DCHS1, EPHB4, FAT4, FGFR1, FGFR2, FLT4, GATA2, GJC2, GNA11, GNA14, GNAQ, HGF, HRAS, IDH1, IDH2, KIF11, KRAS, KRIT1, LZTR1, MAP2K1, MAP3K3, MET, MTOR, NF2, NRAS, PDGFRB, PIEZO1, PIK3CA, PIK3CD, PIK3R1, PIK3R2, PRKACA, PTEN, PTPN14, RASA1, SMAD3, SMO, TEK, TSC1 and TSC2.

Somatic Undergrowth Panel

6 genes sequenced: CDKN1C, GNA11, GNAQ, PIK3CA, PIK3R1 and TEK.

Vascular Anomalies Panel

65 genes sequenced: ACVRL1, ARAF, BRAF, CCBE1, CCM2, CELSR1, CLDN14, CTNNB1, DCHS1, ELMO2, ENG, EPHB4, FAT4, FGFR1, FLT4, FOXC2, GATA2, GDF2, GJA4, GJC2, GLMN, GNA11, GNA14, GNAQ, GNAS, HGF, HRAS, IDH1, IDH2, KDR, KEL, KIF11, KRAS, KRIT1, LZTR1, MAP2K1, MAP2K2, MAP3K3, MET, MTOR, NF1, NRAS, PDCD10, PDGFRB, PIEZO1, PIK3CA, PIK3R1, PIK3R2, PRKACA, PTEN, PTPN11, PTPN14, RASA1, RHOA, SHOC2, SMAD4, SMO, SOS1, SOX18, SPRED1, STAMBP, TEK, TSC1TSC2 and VEGFC.

Custom Panels

Focused and Comprehensive panels available. Please call the laboratory to discuss specific scenarios.